UK - A gene-therapy based cure for haemophilia could be in sight

MelmothTheLost · Dec 14, 2017

Is a cure for haemophilia in sight? 'Mind-blowing' results from a human gene therapy trial offer hope of a life-saving treatment for sufferers of the incurable condition

A cure for haemophilia is one step closer after 'mind-blowing' results from a gene therapy trial, researchers claim.

The trial, led by Barts Health NHS Trust, saw 13 patients injected with a copy of the missing gene, which allowed cells to produce the missing factor.

All 13 patients were able to stop regular treatment for the condition, the 'exciting' study revealed.

http://www.dailymail.co.uk/health/article-5178431/Is-cure-haemophilia.html

meanmaryjean · Dec 14, 2017

I saw this on the BBC site this morning- this is wonderful and gives hope to so many.

UK - A gene-therapy based cure for haemophilia could be in sight

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